Drug Discovery of Therapies for Duchenne Muscular Dystrophy - SLAS Discovery
Rimeporide as a first- in-class NHE-1 inhibitor: Results of a phase Ib trial in young patients with Duchenne Muscular Dystrophy - ScienceDirect
CRISPR technologies for the treatment of Duchenne muscular dystrophy: Molecular Therapy
Progressive muscle proteome changes in a clinically relevant pig model of Duchenne muscular dystrophy | Scientific Reports
Cost of Illness in Patients with Duchenne Muscular Dystrophy in Portugal: The COIDUCH Study | SpringerLink
Peak functional ability and age at loss of ambulation in Duchenne muscular dystrophy - Zambon - 2022 - Developmental Medicine & Child Neurology - Wiley Online Library
DMD genotypes and loss of ambulation in the CINRG Duchenne Natural History Study | Neurology
A new era in the management of Duchenne muscular dystrophy - Korinthenberg - 2019 - Developmental Medicine & Child Neurology - Wiley Online Library
Nutrients | Free Full-Text | Metabogenic and Nutriceutical Approaches to Address Energy Dysregulation and Skeletal Muscle Wasting in Duchenne Muscular Dystrophy | HTML
Muscle membrane integrity in Duchenne muscular dystrophy: recent advances in copolymer-based muscle membrane stabilizers | Skeletal Muscle | Full Text
Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD - ScienceDirect
Consensus on the diagnosis, treatment and follow-up of patients with Duchenne muscular dystrophy | Neurología (English Edition)
BMI-z scores of boys with Duchenne muscular dystrophy already begin to increase before losing ambulation: a longitudinal exploration of BMI, corticosteroids and caloric intake - Neuromuscular Disorders
PDF) Deflazacort vs prednisone/prednisolone for maintaining motor function and delaying loss of ambulation: A post hoc analysis from the ACT DMD trial
Deflazacort, Eteplirsen, and Golodirsen for Duchenne Muscular Dystrophy: Effectiveness and Value
JCM | Free Full-Text | Duchenne Dilated Cardiomyopathy: Cardiac Management from Prevention to Advanced Cardiovascular Therapies | HTML
PDF) Reliability of the walking energy cost test and the six-minute walk test in boys with Duchenne muscular dystrophy
PDF) Comparison of Long-term Ambulatory Function in Patients with Duchenne Muscular Dystrophy Treated with Eteplirsen and Matched Natural History Controls
New variants, challenges and pitfalls in DMD genotyping: implications in diagnosis, prognosis and therapy | Journal of Human Genetics
Clinical characteristics of DMD. a Muscular involvement in the DMD... | Download Scientific Diagram
Prognostic indicators of disease progression in Duchenne muscular dystrophy: A literature review and evidence synthesis | PLOS ONE
The effect of steroid treatment on weight in nonambulatory males with Duchenne muscular dystrophy - Lamb - 2018 - American Journal of Medical Genetics Part A - Wiley Online Library
Pig models for Duchenne muscular dystrophy – from disease mechanisms to validation of new diagnostic and therapeutic concepts - ScienceDirect
Genes | Free Full-Text | Current Outline of Exon Skipping Trials in Duchenne Muscular Dystrophy | HTML
Pig models for Duchenne muscular dystrophy – from disease mechanisms to validation of new diagnostic and therapeutic concepts - Neuromuscular Disorders
